Genetic research uncovers a continuum between diabetes forms, offering insights for precision medicine. Study: Rare variant analyses in 51,256 type 2 diabetes cases and 370,487 controls reveal the ...

Adeno-associated viral (AAV) gene therapy products, which contain a DNA transgene packaged into a protein capsid, have shown tremendous therapeutic potential in recent years for a range of diseases.

Among patients with SLE-associated PAH, those with rare PAH-related gene variants have a unique vasculopathy phenotype and worse outcomes.